News

News Medical on MSN8h
FDA grants orphan drug designation to UAB-developed gene therapy for ALS
The U.S. Food and Drug Administration (FDA) has granted orphan drug designation to a new gene therapy for Amyotrophic Lateral ...
Mirage News13h
FDA Grants Orphan Status to UAB ALS Gene Therapy
The treatment, licensed to Klotho Neurosciences, is based on a technology developed at the Universitat Autònoma de Barcelona (UAB).
ALS News Today9h
ALS gene therapy candidate KLTO‑202 wins orphan drug status
KLTO‑202 is an experimental gene therapy that would deliver the instructions for a protein that may reduce inflammation and oxidative stress.